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CRISPRi
Trinucleotide repeat expansion
Humans
Myositis
Brain
Heart
RNA biology
Genotype phenotype correlation
Cell therapy
Mouse model
Thérapie génique
Transgenic mouse model
DMD
Muscle regeneration
Astrocyte
PABPN1
Inflammation
CMS
LMNA
Biomarkers
Errance diagnostique
Cytoskeleton
Lamin A/C
Myasthenia Gravis MG
Neuromuscular junction
Therapy
Thymus
Fibrosis
Lamin A/C LMNA gene
Myotonic dystrophy
Laminopathy
Glutamate
Mechanotransduction
Clinical trials
Exercise
Treatment
Amyotrophic lateral sclerosis
Fabry disease
Dermatomyositis
Myotonic dystrophy type 1
COVID-19
Regeneration
Alternative splicing
Laminopathies
Muscular dystrophy
Cytokines
Duchenne muscular dystrophy
Transcriptomics
AAV
MBNL
Myotonic Dystrophy
ALS
Neuromuscular diseases
Cancer
Rare neuromuscular diseases
OPMD
Satellite cells
Outcome measures
Myopathy
Neuromuscular disease
Long read sequencing
Centronuclear myopathy
Antisense oligonucleotides
Actin
Congenital muscular dystrophy
RNA interference
Myasthenia gravis
Biomarker
Male
Laminopathie
CTG repeat contractions
Myopathies
Animals
Heart failure
Muscle
Motoneuron
Congenital myopathy
LMNA gene
Nuclear envelope
Cardiomyopathy
Rare diseases
Dilated cardiomyopathy
Myotonic Dystrophy type 1
Autoantibodies
Myogenesis
Becker muscular dystrophy
Calcium
Autoimmune diseases
Aged
Myoblasts
Skeletal muscle
Gene therapy
Autoimmunity
Dynamin 2
FSHD
Satellite cell
Diagnosis
Dystrophin
Autophagy
Aging