Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype - Archive ouverte HAL Access content directly
Journal Articles Science Advances Year : 2020

Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype

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Leslie Weber
  • Function : Author
Giacomo Frati
Tristan Felix
  • Function : Author
Giulia Hardouin
  • Function : Author
Antonio Casini
  • Function : Author
Clara Wollenschlaeger
  • Function : Author
Vasco Meneghini
  • Function : Author
Cecile Masson
  • Function : Author
Anne de Cian
  • Function : Author
Anne Chalumeau
  • Function : Author
Fulvio Mavilio
  • Function : Author
Mario Amendola
Isabelle Andre-Schmutz
Anna Cereseto
  • Function : Author
Wassim El Nemer
Jean-Paul Concordet
  • Function : Author
Marina Cavazzana
Annarita Miccio
  • Function : Author

Dates and versions

mnhn-03099960 , version 1 (06-01-2021)

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Leslie Weber, Giacomo Frati, Tristan Felix, Giulia Hardouin, Antonio Casini, et al.. Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype. Science Advances , 2020, 6 (7), pp.eaay9392. ⟨10.1126/sciadv.aay9392⟩. ⟨mnhn-03099960⟩
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